机译:Chemistry, structure and function of approved oligonucleotide therapeutics
Vanderbilt Univ;
Alnylam Pharmaceut;
DENSITY-LIPOPROTEIN-CHOLESTEROL; ENDOTHELIAL GROWTH-FACTOR; MODIFIED ANTISENSE OLIGONUCLEOTIDES; MEDIATE RNA INTERFERENCE; SPINAL MUSCULAR-ATROPHY; HEPARIN-BINDING DOMAIN; DOUBLE-STRANDED-RNA; IN-VITRO SELECTION; ANTI-VEGF APTAMER; CRYSTAL-STRUCTURE;