Impact of two-year elosulfase alfa treatment on patient-reported outcomes in patients with Morquio syndrome type A: Results from an English managed access agreement

著录项

• 来源
  《Molecular genetics and metabolism 》 |2019年第2期| 共1页
• 作者

  Adam Jacqueline; Cleary Maureen; Hendriksz Christian; Geberhiwot Tarekegn; Hughes Derralynn; Jones Simon A.; Jovanovic Ana; Morrison Alexandra; Murphy Elaine; Vijay Suresh;

  展开▼
• 作者单位

  MPS Commercial Amersham England;

  Great Ormond St Hosp Sick Children London England;

  Univ Pretoria Sch Med Pretoria South Africa;

  New Queen Elizabeth Hosp Birmingham W Midlands England;

  Royal Free London NHS FT &

  UC London England;

  Univ Manchester Manchester Lancs England;

  Salford Royal NHS Fdn Trust Salford Lancs England;

  MPS Commercial Amersham England;

  Natl Hosp Neurol &

  Neurosurg London England;

  Birmingham Childrens Hosp NHS Fdn Trust Birmingham W Midlands England;

  展开▼
• 收录信息
• 原文格式 PDF
• 正文语种 eng
• 中图分类 内分泌腺疾病及代谢病 ;
• 关键词