Cerliponase alfa for the treatment of CLN2 disease in an expanded patient cohort including children younger than three years: Interim results from an ongoing clinical study

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Cerliponase alfa for the treatment of CLN2 disease in an expanded patient cohort including children younger than three years: Interim results from an ongoing clinical study

机译：Cerliponase Alfa用于治疗Cln2疾病的扩张患者群体，包括年龄小于三年的儿童：暂行的临床研究

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《Molecular genetics and metabolism》 |2020年第2期|共1页
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正文语种 eng
中图分类内分泌腺疾病及代谢病;
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1. Cerliponase alfa for the treatment of CLN2 disease in an expanded patient cohort including children younger than three years: Interim results from an ongoing clinical study [J] . Molecular genetics and metabolism . 2020,第2期

机译：Cerliponase Alfa用于治疗Cln2疾病的扩张患者群体，包括年龄小于三年的儿童：暂行的临床研究
2. Persistent treatment effect of cerliponase alfa in children with CLN2 disease: A 3 year update from an ongoing multicenter extension study [J] . Schulz Angela, Specchio Nicola, Gissen Paul, Molecular genetics and metabolism . 2019,第2期

机译：Cerliponase Alfa在CLN2疾病儿童中的持续治疗效果：持续的多中心扩展研究中的3年更新
3. Long-term safety and efficacy of intracerebroventricular enzyme replacement therapy with cerliponase alfa in children with CLN2 disease: interim results from an ongoing multicenter, multinational extension study [J] . Schulz Angela, Specchio Nicola, Gissen Paul, Molecular genetics and metabolism . 2017,第1a2期

机译：患有Cln2疾病儿童Cerliponase Alfa的长期安全性和疗效替代治疗：持续多中心，跨国推广研究中的临时结果
4. Predicting prognosis of stable angina: First results from 5-year prospective cohort study in patients with angiographically proven coronary heart disease in Russia. [C] . Gofman E., Martsevich S., Tolpygina S., International Congress on Coronary Artery Disease . 2011

机译：预测稳定心绞痛的预后：俄罗斯血管造影冠心病患者的5年前瞻性队列研究中的第一个结果。
5. A comparison of selected preoperative coronary artery disease risk factors in patients 40 years or younger and patients over 40 years undergoing coronary artery bypass graft surgery. [D] . Frye, Laurie Perry. 2002

机译：比较40岁以下的患者和40岁以上进行冠状动脉搭桥术的患者的术前选择的冠心病危险因素。
6. Clinical Pharmacokinetics and Pharmacodynamics of Cerliponase Alfa Enzyme Replacement Therapy for CLN2 Disease by Intracerebroventricular Administration [O] . Aryun Kim, Anita Grover, Kevin Hammon, 2021

机译：Cerliponase Alfa的临床药代动力学和药效学Intracebrinallary施用Crn2疾病酶替代疗法
7. Dose selection for intracerebroventricular cerliponase alfa in children with CLN2 disease, translation from animal to human in a rare genetic disease [O] . Kevin Hammon, Greg Hart, Brian R. Vuillemenot, 2021

机译：用ClN2疾病的儿童颅内腔内Cerliponase Alfa的剂量选择，在稀有遗传症中对动物翻译

Cerliponase alfa for the treatment of CLN2 disease in an expanded patient cohort including children younger than three years: Interim results from an ongoing clinical study

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