SUBGROUP ANALYSIS OF PEGVALIASE IN ADULTS WITH PHENYLKETONURIA IN PHASE 3 PRISM STUDIES: EVALUATING EFFICACY AND SAFETY BASED ON PREVIOUS SAPROPTERIN RESPONSE OR DIETARY PHENYLALANINE INTAKE

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• 来源
  《Molecular genetics and metabolism》 |2019年第3期|共1页
• 作者

  Vockley Jerry; Zori Roberto; Thomas Janet A.; Stuy Mary; Burton Barbara K.; Longo Nicola; Rosen Orli; Gu Zhonghu; Olbertz Joy; Weng Haoling H.;

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• 作者单位

  Univ Pittsburgh Pittsburgh PA USA;

  Univ Florida Hlth Gainesville FL USA;

  Univ Colorado Sch Med Aurora CO USA;

  Indiana Univ Indianapolis IN 46204 USA;

  Ann &

  Robert H Lurie Childrens Hosp Chicago Chicago IL 60611 USA;

  Univ Utah Salt Lake City UT USA;

  BioMarin Pharmaceut Inc Novato CA USA;

  BioMarin Pharmaceut Inc Novato CA USA;

  BioMarin Pharmaceut Inc Novato CA USA;

  BioMarin Pharmaceut Inc Novato CA USA;

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• 收录信息
• 原文格式 PDF
• 正文语种 eng
• 中图分类 内分泌腺疾病及代谢病;
• 关键词